Clinical Research Trials : Porphyrias

Porphyrias

Porphyrias

1. NIH: Longitudinal Study of Porphyrias

  • Status: Open
  • PI: Dr. Cynthia Levy
  • Coordinator: Odalys Rodriguez
  • Contact: (305) 243-4648 / obravo@med.miami.edu

2. ALN-AS1-NT-001: A Natural History Study of Acute Hepatic Porphyria (AHP) Patients with Recurrent Attacks

  • Status: Open
  • PI: Dr. Cynthia Levy
  • Coordinator: Odalys Rodriguez
  • Contact: (305) 243-4648 / obravo@med.miami.edu

3. ALN-AS1-003: A Phase 3 Randomized, Double-blind, Placebo-Controlled Mulitcenter Study with an Open-label Extension to Evaluate the Efficacy and Safety of Givosiran in Patients with Actue Hepatic Porphyrias

  • Status: Open
  • PI: Dr. Cynthia Levy
  • Coordinator: Diane Sabogal
  • Contact: (305) 243-1501 / d.sabogal@med.miami.edu

4. MT-7117-A01: A Phase II, Multicenter, Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Efficacy, Safety, And Tolerability of MT-7117 in Subjects with Erythropoietic Protoporphyria

  • Status: Open
  • PI: Dr. Cynthia Levy
  • Coordinator: Tiffannia Grant
  • Contact: (305) 243-4649 / t.grant11@med.miami.edu

5. 7210: Newer Direct_acting Anti-Viral Agents as Sole Therapy of Porphyria Cutanea Tarda in Subjects with Chronic Hepatitis C

  • Status: Open
  • PI: Dr. Cynthia Levy
  • Coordinator: Odalys Rodriguez
  • Contact: Contact: (305) 243-4648 / obravo@med.miami.edu