Clinical Research Trials : Porphyria

Porphyrias

ALN-AS1-NT-001-A Natural History Study of Acute Hepatic Porphyria (AHP) Patients with Recurrent Attacks
o Classification: Porphyria
o Status: Closed enrollment, Open
o PI: Dr. Cynthia Levy
o Coordinator: Katheryn Dae
o Contact: (305) 243-1104 / kqd1@med.miami.edu

NIH – 7201 – Longitudinal Study of Porphyrias
o Classification: Porphyria
o Status: Open enrollment, Open
o PI: Dr. Cynthia Levy
o Coordinator: Edgar Medina
o Contact: (305) 243-0236 / ejm202@med.miami.edu

MT-7117-G01 – A Phase 3, Multicenter, Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Efficacy, Safety, and Tolerability of MT-7117 in Adults and Adolescents with Erythropoietic Protoporphyria or X-Linked Protoporphyria
o Classification: Porphyria
o Status: Open enrollment, Open
o PI: Dr. Cynthia Levy
o Coordinator: Katheryn Dae
o Contact: (305) 243-1104 / kqd1@med.miami.edu